Progress in drug therapy for fragile X syndrome

MEI Lian-ni; HU Chun-chun; XU Qiong

doi:10.11852/zgetbjzz2022-0958

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Chinese Journal of Child Health Care ›› 2023, Vol. 31 ›› Issue (2) : 180-184. DOI: 10.11852/zgetbjzz2022-0958

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Progress in drug therapy for fragile X syndrome

MEI Lian-ni, HU Chun-chun, XU Qiong

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Abstract

Fragile X syndrome (FXS) is a neurodevelopmental disorder that is the most common inherited cause of intellectual disability(ID) and the most prevalent monogenic cause of autism spectrum disorder (ASD). FXS is characterized by cognitive deficits, special facial features, behavioral problems and other multi-system abnormalities. This review combs the drugs that regulate abnormal neurobiology of FXS, in order to provide integrative data of the efficacy and safety of drugs therapy in FXS treatment.

Key words

fragile X syndrome / drug therapy / neurodevelopmental disorder

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MEI Lian-ni, HU Chun-chun, XU Qiong. Progress in drug therapy for fragile X syndrome[J]. Chinese Journal of Child Health Care. 2023, 31(2): 180-184 https://doi.org/10.11852/zgetbjzz2022-0958

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